Hemophilia Gene Therapy: A New Hope for Patients

April 18, 2025

Hemophilia gene therapy is revolutionizing treatment options for individuals like Terence Blue, who recently became the first patient in New England to receive the groundbreaking therapy known as Hemgenix.This innovative approach aims to provide a long-lasting solution to hemophilia B, significantly reducing dependence on daily injections of clotting factor.
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